New legal insights challenge assumptions about pseudonymized data, reshaping data governance and collaboration in rare disease research.

PROMOT advances research on CMS, CM, OPMD, and MFM – four rare neuromuscular diseases – by filling critical data and research gaps

Discover how the PROMOT project is transforming rare neuromuscular disease research through a patient-centered, multi-country approach. Learn about its innovative LEAP platform, interdisciplinary methods, and goals to identify new therapeutic targets.

We’re excited to launch the official website for Performing a Rare Disease-Oriented Master Observational Trial (PROMOT).